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PTC Therapeutics Announces FDA Approval of AADC Deficiency Gene Therapy

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Nov 13, 2024, 15:02 PM PST

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– First-ever FDA approval for gene therapy directly administered to the brain – – Priority review voucher granted – – Broad label including children and adults – – PTC pioneers new approach for CNS drug delivery – WARREN, N.J., Nov. 13, 2024 /PRNewswire/ — PTC Therapeutics, Inc. (NASDAQ:…